Author

Mariana Loperfido

Senior Scientist, AVROBIO - Cited by 640 - Stem Cell Biology - Gene Therapy - Hematopoiesis - Muscular Dystrophy

Biography

Mariana Loperfido, belonging to Translational Cardiomyology, Stem Cell Research Institute, KULeuven, Herestraat 49, 3000 Leuven, Belgium. Interested in the field of Molecular Cloning, Flow Cytometry.
Title
Cited by
Year
A comprehensive single cell transcriptional landscape of human hematopoietic progenitors
D Pellin, M Loperfido, C Baricordi, SL Wolock, A Montepeloso, ...Nature communications 10 (1), 2395, 2019201
238
2019
Chromosomal context and epigenetic mechanisms control the efficacy of genome editing by rare-cutting designer endonucleases
F Daboussi, M Zaslavskiy, L Poirot, M Loperfido, A Gouble, V Guyot, ...Nucleic acids research 40 (13), 6367-6379, 2012201
104
2012
Efficient derivation and inducible differentiation of expandable skeletal myogenic cells from human ES and patient-specific iPS cells
SM Maffioletti, MFM Gerli, M Ragazzi, S Dastidar, S Benedetti, ...Nature protocols 10 (7), 941-958, 2015201
102
2015
Preclinical Safety and Efficacy of Human CD34(+) Cells Transduced With Lentiviral Vector for the Treatment of Wiskott-Aldrich Syndrome
S Scaramuzza, L Biasco, A Ripamonti, MC Castiello, M Loperfido, ...Molecular Therapy 21 (1), 175-184, 2013201
95
2013
Next-generation muscle-directed gene therapy by in silico vector design
S Sarcar, W Tulalamba, MY Rincon, J Tipanee, HQ Pham, H Evens, ...Nature communications 10 (1), 492, 2019201
41
2019
piggyBac transposons expressing full-length human dystrophin enable genetic correction of dystrophic mesoangioblasts
M Loperfido, S Jarmin, S Dastidar, M Di Matteo, I Perini, M Moore, N Nair, ...Nucleic acids research 44 (2), 744-760, 2016201
33
2016
Pluripotent stem cells for gene therapy of degenerative muscle diseases
M Loperfido, H B Steele-Stallard, F Saverio Tedesco, T VandenDriesscheCurrent gene therapy 15 (4), 364-380, 2015201
26
2015
High-throughput analysis of hematopoietic stem cell engraftment after intravenous and intracerebroventricular dosing
RN Plasschaert, MP DeAndrade, F Hull, Q Nguyen, T Peterson, A Yan, ...Molecular Therapy 30 (0), 3209-3225, 2022202
1
2022

Referred From: https://scholar.google.com/citations?user=rt4YSH8AAAAJ&hl=en

Cited by
Citations 640
h-index 7
i10-index 7
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